Defibrotide Sodium — Active Pharmaceutical Ingredient

Defibrotide Sodium is an active pharmaceutical ingredient found in 1 FDA-approved drug product. Forms: SOLUTION. Routes: INTRAVENOUS.

This content is for informational purposes only. Always consult a healthcare professional.

Defibrotide Sodium (1 brand name, 1 dosage form, 1 route)

Available dosage forms: SOLUTION.

Routes of administration: INTRAVENOUS.

Brand Names

  • DEFITELIO

Indications and Usage

DEFITELIO is indicated for the treatment of adult and pediatric patients with hepatic veno-occlusive disease (VOD), also known as sinusoidal obstruction syndrome (SOS), with renal or pulmonary dysfunction following hematopoietic stem-cell transplantation (HSCT).

Contraindications

The use of DEFITELIO is contraindicated in the following conditions: •Concomitant administration with systemic anticoagulant or fibrinolytic therapy [see Warnings and Precautions (5.1)] •Known hypersensitivity to DEFITELIO or to any of its excipients [see Warnings and Precautions (5.2)]

Adverse Reactions

The following adverse reactions are discussed in greater detail in other sections of the labeling: •Hemorrhage [see Warnings and Precautions (5.1)] •Hypersensitivity Reactions [see Warnings and Precautions (5.2)]

Drug Interactions

Antithrombotic Agents DEFITELIO may enhance the pharmacodynamic activity of antithrombotic/fibrinolytic drugs such as heparin or alteplase. Concomitant use of DEFITELIO with antithrombotic or fibrinolytic drugs is contraindicated because of an increased risk of hemorrhage [see Contraindications (4)].

Mechanism of Action

The mechanism of action of defibrotide sodium has not been fully elucidated. In vitro, defibrotide sodium enhances the enzymatic activity of plasmin to hydrolyze fibrin clots. Studies evaluating the pharmacological effects of defibrotide sodium on endothelial cells (ECs) were conducted primarily in the human microvascular endothelial cell line. In vitro, defibrotide sodium increased tissue plasminogen activator (t-PA) and thrombomodulin expression, and decreased von Willebrand factor (vWF) and plasminogen activator inhibitor‑1 (PAI-1) expression, thereby reducing EC activation and increasing EC‑mediated fibrinolysis. Defibrotide sodium protected ECs from damage caused by chemotherapy, tumor necrosis factor-α (TNF-α), serum starvation, and perfusion.

Overdosage

There are no known cases of overdose with DEFITELIO. There is no known antidote for DEFITELIO, and DEFITELIO is not dialyzable. If an overdose occurs, institute general supportive measures.

⚠ Caution
Medical Disclaimer: This information is for educational purposes only. Always consult a healthcare professional before taking any medication.